Business Wire

APR

Share
Rare Diseases: PKU GOLIKE® Debuts in Germany

PKU GOLIKE®, the brand new generation of Phenylalanine (PHe)-free medical food for Phenylketonuria (PKU) dietary management, is now available in Germany and Austria, promoted and distributed directly by APR Applied Pharma Research s.a. (APR) through its local subsidiary, APR Deutschland .

The company has taken advantage of the 33th Annual Meeting of the APS (German Association for Pediatric Metabolic Medicine) in Fulda to showcase to healthcare professionals dealing with PKU the distinctive features of the patented amino acids (AAs) mixtures and the pharma technology enabling it – the Physiomimic™ Technology .

This conference, summoning every year more than 300 pediatricians from Germany, Austria and Switzerland, gives the participants the opportunity to be updated on the most significant advancements in metabolic diseases as well as new therapeutic approaches.

Germany is the biggest country in Europe in terms of prevalence of PKU and population of patients under treatment. According to IMS data, the outlook of the German market for PKU medical food is very positive, showing a growth rate of 9% on a yearly basis, driven mostly by products addressed to patients from 3 years of age onwards.

As confirmed by both German HCPs and patients interviewed during an international market research, palatability (taste and odor) of AA formulations is still one of the key criteria when deciding on a specific AA supplement, as it impacts significantly on the long-term compliance to the dietary treatment and consequently on the overall clinical outcomes.

PKU GOLIKE® , developed by APR and powered by the proprietary Physiomimic™ Technology, could offer a new dietary treatment option to the benefit of patients and HCPs.

During the event, physicians who visited the company booth learned about the key benefit of the innovative AAs mix – the prolonged absorption of AAs , how it makes PKU GOLIKE® a major step in PKU dietary management towards a more efficient AA utilization as well as the scientific data supporting its profile.

Physicians had also the chance to literally taste the unique formulation in special coating micro granules, experiencing how the Physiomimic™ Technology is able to mask the unpleasant taste and odor of free AAs . The audience agreed on the extent of this significant advantage for PKU patients’ compliance to life-long dietary regimen, while appreciating how PKU GOLIKE® could be easily integrated into the daily food routine.

“With PKU GOLIKE® our ambition is to set a new pace in PKU management by providing healthcare professionals, patients and caregivers with a treatment option which can make a real change in their lives.” said Paolo Galfetti, CEO of APR. “In Italy where we launched the product last October with our own sales & marketing organization, we are indeed receiving extremely positive feedbacks from physicians who have already recommended PKU GOLIKE® to a promising number of patients. We are confident this will soon happen also in Germany, a strategic market for us, where again we will be in direct control of the distribution and promotion of the product”.

To further support PKU GOLIKE® awareness among the healthcare professionals dealing with PKU, APR Deutschland is going to participate to the forthcoming congress of the VDD (German Dieticians Association) in Wolfsburg beginning of May, where scientific data will be divulged, while other initiatives are being prepared both on a local and international basis.

About Phenylketonuria or PKU

Phenylketonuria or PKU is a rare, genetic, recessive metabolic disorder affecting about 50.000 people worldwide. PKU is characterized by the deficiency or the malfunctioning of a liver enzyme needed to process phenylalanine (“Phe”). PKU has to be treated through a strict, life-long, low-protein (low-Phe) dietetic treatment combined with a daily assumption of low-protein modified foods and medical food or irreversible mental and physical disabilities will develop.

About PKU GOLIKE®

PKU GOLIKE is an innovative food for special medical purposes (FSMP) consisting of a Phe-free amino acid mixture. For the first time a pharmaceutical technology has been applied to a FSMP and the innovative PKU GOLIKE, engineered with Physiomimic technology™, provides a prolonged-released of amino acids and grants a remarkable taste and odor masking while preventing aftertaste. This prolonged release leads to a physiological absorption of amino acids, similar to dietary proteins, to favor a more efficient amino acid utilization and health benefits. The improvement of free-amino acids' organoleptic features aims to support compliance to the nutritional management of the diet for a better quality of life.

The product line is formed by: PKU GOLIKE PLUS 3-16 & PKU GOLIKE PLUS 16+ with amino acids, vitamins & minerals, and PKU GOLIKE PURE 3+ with only amino acids.

For more information about PKU GOLIKE® and the Physiomimic™ Technology, please visit: www.apr.ch/apr-pharma-products/medical-prescription/genetic-metabolic-disease/

About APR Applied Pharma Research s.a.

APR is a Swiss independent pharma company focused on development and global commercialization of innovative, research-driven products designed to address unmet needs in specialized therapeutic areas and rare diseases. APR combine pharmaceutical development expertise with proprietary drug delivery technologies to realize solutions that meaningfully improve the lives of people with rare diseases and empower families through novel approaches to disease management. A diverse and balanced portfolio of revenue-generating products in all major markets is complemented by a robust pipeline of innovative products at different stages of development for the treatment of recessive metabolic disorders, as well as rare dermatological and ocular diseases. Products are directly commercialized by APR through inhouse sales and marketing teams in strategically important countries across Europe and a growing worldwide network of commercial partners.

Contact:

APR Applied Pharma Research s.a.: Elisabetta Bianchi, Corporate Communication Manager elisabetta.bianchi@apr.ch +41 91 6957020

About Business Wire

Business Wire
Business Wire
101 California Street, 20th Floor
CA 94111 San Francisco

http://businesswire.com

Subscribe to releases from Business Wire

Subscribe to all the latest releases from Business Wire by registering your e-mail address below. You can unsubscribe at any time.

Latest releases from Business Wire

NIKE, Inc. Board of Directors Announces Long-Time Nike Veteran Elliott Hill to Return as President and Chief Executive Officer John Donahoe to Retire from Nike19.9.2024 22:15:00 CEST | Press release

The Board of Directors of NIKE, Inc. (NYSE:NKE) announced today that Elliott Hill will become President and Chief Executive Officer of NIKE, Inc., effective October 14, 2024. Hill will also become a Director of the NIKE, Inc. Board of Directors and a member of the Executive Committee. This press release features multimedia. View the full release here: https://www.businesswire.com/news/home/20240919388699/en/ Incoming NIKE, Inc. President & CEO Elliott Hill (Photo: Business Wire) “I am excited to welcome Elliott back to NIKE. Given our needs for the future, the past performance of the business, and after conducting a thoughtful succession process, the Board concluded it was clear Elliott’s global expertise, leadership style, and deep understanding of our industry and partners, paired with his passion for sport, our brands, products, consumers, athletes, and employees, make him the right person to lead Nike’s next stage of growth,” said Mark Parker, Executive Chairman of NIKE, Inc. “Pers

Andersen Global styrker båndene i Asien med yderligere medlemsvirksomheder19.9.2024 20:53:00 CEST | Pressemeddelelse

Andersen Global tilføjer medlemsvirksomheder i Asien og Stillehavsområdet, hvor VDB Loi-kontorerne i Cambodja og Vietnam tager Andersen-brandet i brug. Andersen i Cambodja og Andersen i Vietnam har under ledelse af Managing Partner Jean Loi og Senior Partner Edwin Vanderbruggen arbejdet i regionen i mere end 10 år. De udbyder en omfattende suite af skatterelaterede og juridiske tjenester, herunder inden for bankvæsen og finans, fusioner og opkøb, virksomhedsrådgivning, skatterådgivning, transfer pricing og tvister og retssager. "Efterhånden som det økonomiske landskab udvikler sig og bliver mere komplekst, går vores kunders forventninger og behov samme vej," siger Edwin. "Ved at blive medlemsvirksomhed i Andersen Global styrker vi vores evne til at levere branchens bedste integrerede service i hele Cambodja og Vietnam. Ved at tage brandet i brug kan vi også accelerere vores vækst, hvilket sætter os i stand til at navigere i et meget indviklet marked med uovertruffen ekspertise." "Med s

Mary Kay Expands Into Kyrgyzstan, Further Elevating Beauty and Empowerment Around the World19.9.2024 19:03:00 CEST | Press release

Mary Kay Inc., a global leader in skin care and cosmetics, is proud to announce its expansion into Kyrgyzstan, marking a significant milestone in its ongoing international growth strategy. This exciting development underscores Mary Kay’s commitment to empowering women and providing innovative, high-quality skincare and beauty products across the globe. This press release features multimedia. View the full release here: https://www.businesswire.com/news/home/20240919159057/en/ Mary Kay’s expansion into Kyrgyzstan marks another step forward in the company’s mission to enrich women’s lives around the world, offering top-tier beauty products and unparalleled business opportunities. (Photo: Mary Kay Inc.) The beauty and personal care market is experiencing robust growth internationally, with sales volume in these categories almost doubling over the past several years. The beauty market is expected to reach approximately $580 billion by 2027, growing by a projected 6 percent per year1 while

Xsolla Partners With AbleGamers for Charity Campaign at TwitchCon 202419.9.2024 19:00:00 CEST | Press release

Collect Limited Edition Pins at TwitchCon and Help Us Raise Up To $10,000 for AbleGamers Xsolla, a global video game commerce company, is excited to announce its collaboration with AbleGamers for an impactful charity campaign at TwitchCon 2024. This partnership aims to further AbleGamers' mission of improving accessibility in gaming for individuals with disabilities through an interactive and meaningful activation. This press release features multimedia. View the full release here: https://www.businesswire.com/news/home/20240919722398/en/ (Graphic: Xsolla) Attendees who visit the Xsolla booth (Booth 1515-SW) at TwitchCon will have the exclusive opportunity to claim one of two specially designed charity pins. By sharing a photo of their pin on their social channels on Instagram, Facebook, or Twitter using the hashtags #LightstreamAble and #XsollaAble, participants will help raise funds for AbleGamers. For every qualifying social post, Xsolla and its partners will donate $5 to AbleGamers

Sandvine Announces New Ownership and Capital Infusion19.9.2024 18:38:00 CEST | Press release

New ownership group commits new financingWill help to support reorientation of business and continued customer service and technological innovation Sandvine (the “Company”), a market-leading provider of Over-the-Top (OTT) Application Classification and Quality of Experience (QoE) solutions, today announced that it has been acquired by a group of leading US investment firms that previously were, and continue to be, lenders to the Company. In connection with this change of control transaction, the lenders agreed to reduce the Company’s total outstanding debt significantly. Following the change of control transaction, on September 13, 2024, these investors also entered into a binding agreement to provide new capital to Sandvine. The financing is expected to close in September 2024 and will strengthen the Company’s balance sheet. These enhancements to Sandvine’s financial position accompany its recently announced reorientation of its business model to focus on serving customers in large de

In our pressroom you can read all our latest releases, find our press contacts, images, documents and other relevant information about us.

Visit our pressroom
HiddenA line styled icon from Orion Icon Library.Eye